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Hope for Future Treatment

Both doctors and pharmaceutical companies are working on creating the next big thing for the treatment of your bleeding disorder. Many new treatments are under investigation and offer hope for improving the lives of individuals like you who live with a bleeding disorder.

Most everyone can agree that new and improved bleeding disorder medications cannot come fast enough. But getting a new drug to those who need it can take a great deal of time. It takes time for doctors and pharmaceutical companies to discover a new drug. Once discovered, the drug must be approved and licensed by the US Food and Drug Administration, which requires that the drug go through a series of clinical trials. Each phase of a clinical trial helps determine the drug’s safety, efficacy, optimal dosage, and side effects. It takes approximately 5 years for a drug to be approved once it has begun clinical trials. The good news is that there are now more drugs in the development pipeline than in the past few decades.

A few things that are expected to come along in the near future:

  • Products that last longer in the bloodstream.
  • A recombinant von Willebrand factor (vWF) product (for individuals with type 3 von Willebrand disease [VWD]).
  • Drugs that treat diseases caused by specific genetic mutations, such as individuals who have hemophilia A and B with a mutation that halts clotting factor production early.
  • Drugs that treat various rare clotting factor deficiencies.
To learn more about what’s on the horizon in drugs for bleeding disorders, go to www.HemAware.org